Freedom of Information Request: 0112 2019/20

Q1. Within your trust how many patients have been treated, in the past 3 months [latest 3 months available] for Fabry Disease?

61

Q2. Of these patients [from question 1], how many have been treated with the following [please state the number per treatment]

Replagal (agalsidase alpha) 19

Fabrazyme (agalsidase beta) 11    

Galafold (migalastat) 28

Other [please state which treatments] 3 clinical trial IMP

Q3. Within your trust how many patients have been treated, in the past 3 months [latest 3 months available] for Gaucher’s Disease?

10

Q4. Of these patients [from question 3], how many have been treated with the following [please state the number per treatment]

VPRIV (velaglucerase alfa) 2         

Cerezyme (imiglucerase) 3           

Cerdelga (eliglustat) 5     

Zavesca (miglustat) 0       

Other [please state which treatments] 0

If you are unable to link diagnosis and treatment, please state the number of patients on each of the following treatments;

Replagal (agalsidase alpha)

Fabrazyme (agalsidase beta)     

Galafold (migalastat)    

VPRIV (velaglucerase alfa)         

Cerezyme (imiglucerase)           

Cerdelga (eliglustat)     

Zavesca (miglustat)       

Not applicable.