Freedom of Information Request: 0402 2019/20
Q1. How many NEW patients have been diagnosed for Fabry Disease in the past 3 months [latest 3 months available]?
7 patients
Q2. How many NEW patients have been diagnosed for Gaucher’s Disease in the past 3 months [latest 3 months available]?
1 patient
Q3. How many NEW patients have been diagnosed for MPS II (Hunter Syndrome) in the past 3 months [latest 3 months available]?
None
Q4. Please state the number of patients treated in the past 3 months [latest 3 months available] on each of the following treatments, regardless of diagnosis;
Replagal (agalsidase alpha) – 20
Fabrazyme (agalsidase beta) – 13
Galafold (migalastat) – 28
VPRIV (velaglucerase alfa) – 2
Cerezyme (imiglucerase) – 3
Cerdelga (eliglustat) – 5
Zavesca (miglustat) – 1